Organization Overview
Timeline
Active Ingredients
Indications
Clinical Trials
Targets and Mechanisms
Alternative names
verbrinacogene setparvovec (2 trials)
flt190 (2 trials)
flt201 (1 trial)
Fabry Disease (Phase 2)
Hemophilia A (Phase 3)
Hemophilia B (Phase 3)
Lysosomal Storage Diseases (Phase 2)
Trials (5 total)
Trial APIs (3 total)