Organization Overview
Timeline
Active Ingredients
Indications
Clinical Trials
Targets and Mechanisms
Laronidase (Aldurazyme) (4 trials)
Lysosomal Storage Diseases (Phase 1)
Mucopolysaccharidoses (Phase 1)
Mucopolysaccharidosis I (Phase 1)
Spinal Cord Compression (Phase 1)
Syndrome (Phase 1)
Trials (4 total)
Trial APIs (1 total)