Organization Overview
Timeline
Active Ingredients
Indications
Clinical Trials
Targets and Mechanisms
Alternative names
autologous cd34+ cell-enriched fraction that contains cells transduced with lentiviral vector/alpha-galactosidase a (1 trial)
autologous cd34 hscs transduced ex vivo with cd11b lv encoding human ids tagged with apoeii (1 trial)
avr-rd-02 (1 trial)
Fabry Disease (Phase 2)
Gaucher Disease (Phase 2)
Trials (3 total)
Trial APIs (3 total)