Organization Overview
Timeline
Active Ingredients
Indications
Clinical Trials
Targets and Mechanisms
Alternative names
aav5-rpgr (2 trials)
aav2haqp1 (2 trials)
aav-gad (2 trials)
aav-rpgr (1 trial)
raav.hcnga3 (3 trials)
Color Vision Defects (Phase 2)
Retinitis (Phase 2)
Retinitis Pigmentosa (Phase 2)
Xerostomia (Phase 2)
Trials (10 total)
Trial APIs (5 total)