Organization Overview
Timeline
Active Ingredients
Indications
Clinical Trials
Targets and Mechanisms
Alternative names
ambroxol (1 trial)
pyrimethamine (daraprim) (1 trial)
Gangliosidoses (Phase 1)
Gangliosidoses, GM2 (Phase 1)
Gaucher Disease (Phase 2)
Sandhoff Disease (Phase 1)
Tay-Sachs Disease (Phase 1)
Trials (2 total)
Trial APIs (2 total)