Organization Overview
Alternative names
Adrenoleukodystrophy (Phase 1)
alpha-Mannosidosis (Phase 1)
Autism Spectrum Disorder (Phase 2)
Autistic Disorder (Phase 2)
Brain Diseases (Phase 1)
Brain Diseases, Metabolic (Phase 1)
Brain Diseases, Metabolic, Inborn (Phase 1)
Brain Injuries (Phase 2)
Cerebral Palsy (Phase 2)
Child Development Disorders, Pervasive (Phase 2)
Coronavirus Infections (Phase 2)
Disease (Phase 2)
Leukodystrophy, Globoid Cell (Phase 1)
Leukodystrophy, Metachromatic (Phase 1)
Mannosidase Deficiency Diseases (Phase 1)
Metabolic Diseases (Phase 1)
Mucopolysaccharidoses (Phase 1)
Mucopolysaccharidosis II (Phase 1)
Neuronal Ceroid-Lipofuscinoses (Phase 1)
Niemann-Pick Diseases (Phase 1)
Niemann-Pick Disease, Type A (Phase 1)
Niemann-Pick Disease, Type C (Phase 1)
Osteoarthritis (Phase 3)
Pelizaeus-Merzbacher Disease (Phase 1)
Pick Disease of the Brain (Phase 1)
Sandhoff Disease (Phase 1)
Sepsis (Phase 3)
Severe Acute Respiratory Syndrome (Phase 2)
Stroke (Phase 2)
Tay-Sachs Disease (Phase 1)
Toxemia (Phase 3)