Organization Overview
Timeline
Active Ingredients
Indications
Clinical Trials
Targets and Mechanisms
Alternative names
lys-saf302 (1 trial)
lys-gm101 (1 trial)
saf-301 (2 trials)
Gangliosidoses (Phase 2)
Gangliosidosis, GM1 (Phase 2)
Mucopolysaccharidoses (Phase 3)
Mucopolysaccharidosis III (Phase 3)
Trials (4 total)
Trial APIs (3 total)