Diseases [C] » Hemic and Lymphatic Diseases [C15] » Hematologic Diseases » Anemia » Anemia, Aplastic » Anemia, Hypoplastic, Congenital
Diseases [C] » Hemic and Lymphatic Diseases [C15] » Hematologic Diseases » Bone Marrow Diseases » Bone Marrow Failure Disorders » Congenital Bone Marrow Failure Syndromes » Anemia, Hypoplastic, Congenital
Diseases [C] » Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16] » Genetic Diseases, Inborn » Anemia, Hypoplastic, Congenital
Description
An inborn condition characterized by deficiencies of red cell precursors that sometimes also includes LEUKOPENIA and THROMBOCYTOPENIA. MeSH
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Subtype Terms (2)
Anemia, Diamond-Blackfan
38 drugs (23 approved, 15 experimental)
Fanconi Anemia
48 drugs (27 approved, 21 experimental)
Organization Involved with Phase 2 Indications (1)
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UMLS Data
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