Diseases [C] » Hemic and Lymphatic Diseases [C15] » Hematologic Diseases » Blood Coagulation Disorders » Blood Coagulation Disorders, Inherited
Diseases [C] » Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16] » Genetic Diseases, Inborn » Blood Coagulation Disorders, Inherited
Description
Hemorrhagic and thrombotic disorders that occur as a consequence of inherited abnormalities in blood coagulation. MeSH
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Subtype Terms (19)
Activated Protein C Resistance
2 approved drugs
Afibrinogenemia
2 approved drugs
Antithrombin III Deficiency
3 drugs (2 approved, 1 experimental)
Factor VII Deficiency
7 drugs (3 approved, 4 experimental)
Factor X Deficiency
1 approved drug
Factor XI Deficiency
1 approved drug
Factor XIII Deficiency
1 approved drug
Hemophilia A
99 drugs (49 approved, 50 experimental)
Hemophilia B
49 drugs (18 approved, 31 experimental)
Hermanski-Pudlak Syndrome
12 approved drugs
Hypoprothrombinemias
3 approved drugs
Protein C Deficiency
1 approved drug
Thrombasthenia
10 drugs (8 approved, 2 experimental)
von Willebrand Diseases
16 drugs (8 approved, 8 experimental)
Wiskott-Aldrich Syndrome
34 drugs (25 approved, 9 experimental)
Organization Involved with Phase 2 Indications (2)
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UMLS Data
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