Active Ingredient History
Alglucosidase alfa, sold under the brand name Myozyme among others, is an enzyme replacement therapy (ERT) orphan drug for treatment of Pompe disease, a rare lysosomal storage disorder (LSD). Chemically, the drug is an analog of the enzyme that is deficient in patients affected by Pompe disease, alpha-glucosidase. It is the first drug available to treat this disease. Wikipedia
Drug Pricing (per unit)
Note: This drug pricing data is preliminary, incomplete, and may contain errors.
Organization | Org Type | FDA approvals | Clinical Trials involvement | Org ID | Force Sort |
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Organization | Org Type | FDA approvals | Clinical Trials involvement | Org ID | Force Sort |
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Genetic Diseases, Inborn (Phase 4)
Glycogen Storage Disease (Phase 4)
Glycogen Storage Disease Type II (Phase 4)
Sucrase-Isomaltase Complex (Phase 4)
Trial | Phase | Start Date | Organizations | Indications |
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